Drug 'mends' muscular dystrophy
An experimental drug may be able to compensate for the genetic error responsible for some cases of Duchenne Muscular Dystrophy, US scientists hope. In rodents, the drug PTC124 was able to restore the muscle function normally lost in this disease, Nature reports. Trials have already begun in humans, although the results will take years. The drug works by allowing cells to read through certain mistakes in the genetic code for a protein - dystrophin - missing in 15% of patients with DMD.